Publication · Feb 2021 · PDF
Science
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These pages contain non-exhaustive scientific information about uses of products that have not yet been approved by regulatory authorities, as their efficacy and safety for these uses have not yet been established. The information is provided for educational and scientific exchange purposes, and does not suggest products should be used in a manner not consistent with their respective label approved by the regulatory authorities, which may differ by geography. Any publication reflects the state of knowledge at the time it was published. The information is not medical advice and cannot replace the independent medical judgement of a healthcare professional.
Publication · Feb 2021
Patient and family experience with ATTR-CM and ATTR-PN: two focus groups
Publication · Jul 2019
Transthyretin stabilization by AG10 in symptomatic ATTR-CM
Publication · Jun 2019
First-in-human study of AG10: phase 1 in healthy volunteers
Publication · 2019 · PDF
Orphanet Journal of Rare Diseases, Achondroplasia: A Comprehensive Clinical Review
Publication · Aug 2018
Enthalpy-driven stabilization of TTR by AG10 mimics a protective genetic variant
Publication · Dec 2016 · PDF
Developmental Dynamics, Achondroplasia: Development, Pathogenesis, and Therapy
Publication · May 2013
AG10 inhibits amyloidogenesis and cellular toxicity of V122I transthyretin
Publication · Aug 2011