PRESENTATION · Sep 2025 · PDF
Science
Explore conditions, clinical trials, and the latest research.
These pages contain non-exhaustive scientific information about uses of products that have not yet been approved by regulatory authorities, as their efficacy and safety for these uses have not yet been established. The information is provided for educational and scientific exchange purposes, and does not suggest products should be used in a manner not consistent with their respective label approved by the regulatory authorities, which may differ by geography. Any publication reflects the state of knowledge at the time it was published. The information is not medical advice and cannot replace the independent medical judgement of a healthcare professional.
PUBLICATION · Feb 2021 · PDF
Bone, Lifetime Impact of Achondroplasia: Current Evidence and Perspectives on the Natural History
PUBLICATION · Jan 2019 · PDF
Orphanet Journal of Rare Diseases, Achondroplasia: A Comprehensive Clinical Review
PUBLICATION · Dec 2016 · PDF