Science / Canavan Disease / Presentations & Publications

Presentations & Publications

Canavan Disease

PRESENTATION · Apr 2025 · PDF

BBIO - Canavan GTx BBP-812 - NTSAD 2025 - CANaspire Program Updates

PUBLICATION · Mar 2025

Pediatric Neurology, Feasibility, Acceptability, and Reliability of Remote Motor Assessment in Children with Canavan Disease

PUBLICATION · Jan 2025

Human Gene Therapy, Urine N-Acetylaspartate Distinguishes Phenotypes in Canavan Disease

PRESENTATION · Dec 2024 · PDF

Canavan GTx BBP-812 - ESGCT 2024 - Positive Data from High Dose Cohort of Phase 1/2 CANaspire Study

PRESENTATION · Dec 2023 · PDF

Canavan GTx BBP-812 - Neurology for Science 2023 - CANaspire Phase 1/2 Study

PRESENTATION · Dec 2023 · PDF

Canavan GTx BBP-812 - ASGCT 2023 - CANaspire Initial Biomarker and Clinical Findings