PRESENTATION · Dec 2023 · PDF
Science
Explore conditions, clinical trials, and the latest research.
These pages contain non-exhaustive scientific information about uses of products that have not yet been approved by regulatory authorities, as their efficacy and safety for these uses have not yet been established. The information is provided for educational and scientific exchange purposes, and does not suggest products should be used in a manner not consistent with their respective label approved by the regulatory authorities, which may differ by geography. Any publication reflects the state of knowledge at the time it was published. The information is not medical advice and cannot replace the independent medical judgement of a healthcare professional.
PRESENTATION · Dec 2023 · PDF
Canavan GTx BBP-812 - ASGCT 2023 - CANaspire Initial Biomarker and Clinical Findings
PRESENTATION · Dec 2023 · PDF
Acoramidis - ESC 2023 - ATTRibute-CM-Efficacy and Safety of Acoramidis in Transthyretin Amyloid Cardiomyopathy
PRESENTATION · Dec 2023 · PDF
Infigratinib - ENDO 2023 - Murine Models in Achondroplasia and Hypochondroplasia
PRESENTATION · Dec 2023 · PDF
Encaleret - ADH1 - ASBMR 2023 CALIBRATE Phase 3 Study Design
PRESENTATION · Dec 2023 · PDF
BBP-418 for LGMD2I/R9 - MDA 2023 - Poster - Phase 2 Data at 15 Months
PRESENTATION · Dec 2023 · PDF
Encaleret - ADH1 - ENDO 2023 18 Month Phase 2b Data
PRESENTATION · Dec 2023 · PDF
BBP-418 for LGMD2I/R9 - MDA 2023 - Preliminary Data on Bioassay Measuring αDG
PRESENTATION · Dec 2023 · PDF