Science
Explore conditions, clinical trials, and the latest research.
These pages contain non-exhaustive scientific information about uses of products that have not yet been approved by regulatory authorities, as their efficacy and safety for these uses have not yet been established. The information is provided for educational and scientific exchange purposes, and does not suggest products should be used in a manner not consistent with their respective label approved by the regulatory authorities, which may differ by geography. Any publication reflects the state of knowledge at the time it was published. The information is not medical advice and cannot replace the independent medical judgement of a healthcare professional.
PRESENTATION · Apr 2025 · PDF
BBIO - Canavan GTx BBP-812 - NTSAD 2025 - CANaspire Program Updates
PRESENTATION · Apr 2025 · PDF
Acoramidis TTR - ACC 2025 - Addition of Another TTR Stabilizer Did Not Further Increase Serum TTR Levels
PRESENTATION · Apr 2025 · PDF
Acoramidis TTR - ACC 2025 - Improvements in Serum TTR Levels in Variant Population
PRESENTATION · Apr 2025 · PDF
Acoramidis TTR - ACC 2025 - Pre-specified NT-proBNP Sensitivity Analyses
PRESENTATION · Apr 2025 · PDF
Acoramidis TTR - ACC 2025 - Improvements in NYHA Class at Month 30 Versus Placebo
PRESENTATION · Mar 2025 · PDF