PRESENTATION · Sep 2025 · PDF

Acoramidis-HFSA-2025-Cardiac-Conduction-abnormalities

PRESENTATION · Sep 2025 · PDF

Encaleret - Chronic Hypoparathyroidism - Proof of Concept Study in Post-Surgical Hypoparathyroidism

PRESENTATION · Sep 2025 · PDF

Infigratinib - Crouzon/Pfeiffer Syndromes - Preclinical Improvement in Skull Measures

PRESENTATION · Sep 2025 · PDF

Infigratinib - Hypochondroplasia - Preclinical Improvement in Bone Growth

PRESENTATION · Aug 2025 · PDF

BBIO - Acoramidis TTR- ESC 2025 - Improvement in NT-proBNP

PRESENTATION · Aug 2025 · PDF

BBIO - Acoramidis TTR - ESC 2025 - Stable/Improved NAC at Month 30

PRESENTATION · Jul 2025 · PDF

ADH1 - ENDO 2025 - Baseline Characteristics of Pediatric Participants in the CLARIFY Disease Monitoring Study

PRESENTATION · Jul 2025 · PDF

Encaleret - ADH1 - ENDO 2025 - Phase 2 Over 42 Months Data Results

PRESENTATION · Jul 2025 · PDF

Encaleret - ADH1 - ENDO 2025 - CALIBRATE-PEDS Phase 2/3 Study Design

PRESENTATION · Jul 2025 · PDF

ADH1- ENDO 2025 - Findings from Sponsored Genetic Testing Program Show Gain-of-function CASR Variants Identified as a Major Genetic Contributor of Non-Surgical Hypoparathyroidism