PRESENTATION · Dec 2023 · PDF

Canavan GTx BBP-812 - ASGCT 2023 - CANaspire Initial Biomarker and Clinical Findings

PRESENTATION · Dec 2023 · PDF

Acoramidis - ESC 2023 - ATTRibute-CM-Efficacy and Safety of Acoramidis in Transthyretin Amyloid Cardiomyopathy

PRESENTATION · Dec 2023 · PDF

Infigratinib - ENDO 2023 - Murine Models in Achondroplasia and Hypochondroplasia

PRESENTATION · Dec 2023 · PDF

Encaleret - ADH1 - ASBMR 2023 CALIBRATE Phase 3 Study Design

PRESENTATION · Dec 2023 · PDF

BBP-418 for LGMD2I/R9 - MDA 2023 - Poster - Phase 2 Data at 15 Months

PRESENTATION · Dec 2023 · PDF

Acoramidis - ESC 2023 - Acoramidis Produces Near-Complete TTR Stabilization in Variant ATTR Patients that is Greater than that Achieved with Tafamidis

PRESENTATION · Dec 2023 · PDF

Encaleret - ADH1 - ENDO 2023 18 Month Phase 2b Data

PRESENTATION · Dec 2023 · PDF

BBP-418 for LGMD2I/R9 - MDA 2023 - Preliminary Data on Bioassay Measuring αDG

PRESENTATION · Dec 2023 · PDF

ADH1 - ENDO 2023 Preliminary Results from Genetic Testing Program

PRESENTATION · Dec 2023 · PDF

BBP-418 for LGMD2I/R9 - Novel Bioassay, Phase 2 Data and Phase 3 Trial Design in LGMD2I